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The Netherlands. Tel: +31 88 166 7000 (Address, Including ZIP Code, and Telephone Number, Including Area Code, of Registrant’s Principal Executive Offices) Indicate by check mark whether the registrant files or will file annual reports under cover of Form 20-F or Form 40-F. Based on the unique proprietary RNA repair platform technologies, they are growing their pipeline with patients and their loved ones in mind. www.proqr.com.

About us; Vision 2023; Leadership; Careers; Contact; Science & Pipeline. Research and development pipeline; Clinical Trials. QR-1123 Aurora phase 1/2 study for adRP; Sepofarsen ILLUMINATE phase 2/3 study for LCA10; QR-421a STELLAR phase 1/2 study for Usher syndrome; Sepofarsen INSIGHT – phase 1b/2 study for LCA10; Sepofarsen Key Updates ProQR’s drug candidate QR-313 for dystrophic epidermolysis bullosa (DEB) receives orphan drug designation from the FDA , representing the fifth program in the Company’s pipeline to receive ODD in the U.S. The Company will be presenting pre-clinical data for QR-313 at two European We are ProQR Therapeutics, a clinical stage biotechnology company. We develop RNA therapies for severe genetic rare diseases, with a high need for new medici LEIDEN, Netherlands & CAMBRIDGE, Mass., March 24, 2021 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq: PRQR) (the "Company"), a company dedicated to changing lives through the creation of transformative RNA therapies for inherited retinal diseases (IRDs), today announced results from a planned analysis of its Phase 1/2 Stellar trial of QR-421a in adults with Usher syndrome and non In an interview with PharmaShots, Daniel A. de Boer of ProQR shared his views on P-II/III pivotal trial of Sepofarsen to treat the root cause of a rare eye disease, Leber congenital amaurosis 10 (LCA10) Shots: The Illuminate P-II/III trial of sepofarsen is a double-masked, randomized, controlled, multiple-dose study to evaluate if sepofarsen is effective […] PROQR THERAPEUTICS N.V. Zernikedreef 9.

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The company’s current pipeline includes potential treatments for rare genetic diseases including Leber's congenital amaurosis, (LCA10) dystrophic epidermolysis bullosa and Usher syndrome. 2019-03-13 · The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited ProQR intends to use the net proceeds from the offering, together with its existing cash and cash equivalents, to advance clinical development of its product candidates, to progress its other pipeline candidates, to advance its RNA-editing technology platforms, and for working capital and other general corporate purposes. 2021-03-24 · Shares of ProQR Therapeutics (NASDAQ:PRQR) were trading higher on Wednesday after the company released positive results from a clinical trial for one of its leading pipeline candidates, QR-421a. The programs in ProQR’s pipeline utilize the RNA oligonucleotide technology platform that repairs the genetic defect in the RNA to address the underlying cause of genetic diseases.

ProQR In-licenses Worldwide Rights to Ophthalmology Drug

Visit website. ProQR our strategy to create a well-diversified pipeline of medicine candidates in several therapeutic areas.

Research and development pipeline; Clinical Trials.
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We are on a mission The Dutch biotech has firmed up its finances as its promising pipeline of RNA therapies for rare genetic eye disease starts to move through the clinic.

The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital amaurosis 10 LEIDEN, the Netherlands & CAMBRIDGE, Mass., Jan. 29, 2019 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (PRQR), a company dedicated to changing lives through the creation of transformative RNA About ProQR ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development. “Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR.
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ProQR In-licenses Worldwide Rights to Ophthalmology Drug

We are ProQR, a biotechnology company dedicated to changing lives by developing RNA therapies for rare genetic diseases. We focus our drug development mainly on a group of blinding disorders affecting the retina, called inherited retinal diseases. We are on a mission The Dutch biotech has firmed up its finances as its promising pipeline of RNA therapies for rare genetic eye disease starts to move through the clinic. ProQR Raises $90m To Advance Eye Disease Pipeline :: Scrip “We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA therapies to potentially help children, adults, and families who are affected by blindness caused by USH2A mutations and other rare inherited retinal diseases.” Phase 1/2 Stellar trial of QR-421a Shares of ProQR Therapeutics (NASDAQ:PRQR) were trading higher on Wednesday after the company released positive results from a clinical trial for one of its leading pipeline candidates, QR-421a.

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The programs in ProQR’s pipeline utilize the RNA oligonucleotide technology platform that repairs the genetic defect in the RNA to address the underlying cause of genetic diseases.

The company's current pipeline Based on its unique proprietary RNA repair platform technologies, ProQR Therapeutics is growing its pipeline with patients and loved ones in mind.